Relative persistence of AAV serotype 1 vector genomes in dystrophic muscle
نویسندگان
چکیده
منابع مشابه
Relative persistence of AAV serotype 1 vector genomes in dystrophic muscle
The purpose of this study was to assess the behavior of pseudotyped recombinant adeno-associated virus type 1 (rAAV2/1) vector genomes in dystrophic skeletal muscle. A comparison was made between a therapeutic vector and a reporter vector by injecting the hindlimb in a mouse model of Limb Girdle Muscular Dystrophy Type 2D (LGMD-2D) prior to disease onset. We hypothesized that the therapeutic ve...
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ژورنال
عنوان ژورنال: Genetic Vaccines and Therapy
سال: 2008
ISSN: 1479-0556
DOI: 10.1186/1479-0556-6-14